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Acute Myeloid Leukemia Case after Gene Therapy for Sickle Cell Disease.
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Acute Myeloid Leukemia Case after Gene Therapy for Sickle Cell Disease.
Acute Myeloid Leukemia Case after Gene Therapy for Sickle Cell Disease. N Engl J Med. 2022 01 13; 386(2):138-147.
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PubMed
subject areas
Adult
Anemia, Sickle Cell
beta-Globins
Carcinogenesis
Female
Gene Expression
Genetic Therapy
Genetic Vectors
Hematopoietic Stem Cell Transplantation
Humans
Lentivirus
Leukemia, Myeloid, Acute
Risk Factors
Sequence Analysis, RNA
Transgenes
Transplantation, Autologous
authors with profiles
Jennifer Joi Jaroscak